gene therapy

FDA
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FDA investigates 2 deaths after Sarepta Duchenne gene therapy

The agency is investigating two Duchenne muscular dystrophy patient deaths following treatment with Sarepta Therapeutics’ Elevidys.
Angus Liu Jun 25, 2025 10:26am
Fabry disease

Cash-strapped Sangamo seeks partner for new gene therapy

Jun 24, 2025 11:53am
Reorganization team change restructure

Industry disappointed as FDA reportedly puts Verdun on leave

Jun 20, 2025 1:53am
Redbrick building with Sarepta name and logo
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2nd patient dies after Sarepta's DMD gene therapy Elevidys

Jun 16, 2025 10:58am
An artists depiction of DNA molecules made up of tiny particles

RegenXBio links DMD gene therapy to improved outcomes

Jun 5, 2025 8:52am
Make a delay and accumulation of outstanding tasks Full stop

Rocket crashes as gene therapy patient dies, FDA imposes hold

May 27, 2025 9:49am